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Respirology, Rare Diseases
Residual Function Mutations in Cystic Fibrosis: An Important Target for Treatment – Certificate of Completion
Cystic fibrosis remains one of the most common life-shortening rare diseases, affecting about 85,000 individuals worldwide. Novel therapeutic approaches, including CFTR modulators, can offer clinical benefit to people with CF, producing improvements across numerous relevant endpoints.
DURATION
1 hr
PROFESSION
Specialist
# OF CREDITS
1
ACCREDITATION
Certificate of Completion
EXPIRY DATE
2021-03-29
Cystic fibrosis remains one of the most common life-shortening rare diseases, affecting about 85,000 individuals worldwide. Novel therapeutic approaches, including CFTR modulators, can offer clinical benefit to people with CF, producing improvements across numerous relevant endpoints.
Faculty
Margarida D Amaral
Professor, Faculty of Sciences
University of Lisbon, Portugal
Peter Middleton
Centre Director, Adult CF Service, Westmead Hospital, Sydney
Clinical Professor, University of Sydney
Chief Investigator, Ludwig Engel Centre for Respiratory Research,
Westmead Institute for Medical Research, Sydney